NICE (UK) negative for Brineura (cerliponase alfa) for treating neuronal ceroid lipofuscinosis type 2 – BioMarin
NICE(UK): Cerliponase alfa is not recommended, within its marketing authorisation, for treating neuronal ceroid lipofuscinosis type 2 (CLN2; also known as tripeptidyl peptidase 1 deficiency). This recommendation is not intended… read more.
